Search details
1.
Expanded circulating hematopoietic stem/progenitor cells as novel cell source for the treatment of TCIRG1 osteopetrosis.
Haematologica
; 106(1): 74-86, 2021 01 01.
Article
in English
| MEDLINE | ID: mdl-31949009
2.
Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation.
J Allergy Clin Immunol
; 142(3): 928-941.e8, 2018 09.
Article
in English
| MEDLINE | ID: mdl-29241731
3.
Murine Rankl-/- Mesenchymal Stromal Cells Display an Osteogenic Differentiation Defect Improved by a RANKL-Expressing Lentiviral Vector.
Stem Cells
; 35(5): 1365-1377, 2017 05.
Article
in English
| MEDLINE | ID: mdl-28100034
4.
Dual-regulated lentiviral vector for gene therapy of X-linked chronic granulomatosis.
Mol Ther
; 22(8): 1472-1483, 2014 Aug.
Article
in English
| MEDLINE | ID: mdl-24869932
5.
Cysteine and hydrophobic residues in CDR3 serve as distinct T-cell self-reactivity indices.
J Allergy Clin Immunol
; 144(1): 333-336, 2019 07.
Article
in English
| MEDLINE | ID: mdl-31053347
6.
Lentiviral vectors for the treatment of primary immunodeficiencies.
J Inherit Metab Dis
; 37(4): 525-33, 2014 Jul.
Article
in English
| MEDLINE | ID: mdl-24619149
7.
HyperIgE in hypomorphic recombination-activating gene defects.
Curr Opin Immunol
; 80: 102279, 2023 02.
Article
in English
| MEDLINE | ID: mdl-36529093
8.
Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations.
Front Immunol
; 14: 1268620, 2023.
Article
in English
| MEDLINE | ID: mdl-38022635
9.
Osteoclast rich osteopetrosis due to defects in the TCIRG1 gene.
Bone
; 165: 116519, 2022 12.
Article
in English
| MEDLINE | ID: mdl-35981697
10.
Autosomal recessive osteopetrosis: mechanisms and treatments.
Dis Model Mech
; 14(5)2021 05 01.
Article
in English
| MEDLINE | ID: mdl-33970241
11.
Innovative Cell-Based Therapies and Conditioning to Cure RAG Deficiency.
Front Immunol
; 11: 607926, 2020.
Article
in English
| MEDLINE | ID: mdl-33329604
12.
One Disease, Many Genes: Implications for the Treatment of Osteopetroses.
Front Endocrinol (Lausanne)
; 10: 85, 2019.
Article
in English
| MEDLINE | ID: mdl-30837952
13.
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Sci Transl Med
; 9(411)2017 Oct 11.
Article
in English
| MEDLINE | ID: mdl-29021165
14.
Serratia marcescens osteomyelitis in a newborn with chronic granulomatous disease.
Pediatr Infect Dis J
; 32(8): 926, 2013 Aug.
Article
in English
| MEDLINE | ID: mdl-23518820
Results
1 -
14
de 14
1
Next >
>>